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STS-CHAPTER 5- GENE THERAPY

STS-CHAPTER 5- GENE THERAPY
25問 • 1年前
  • Anndrea S. Galupo
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  • 1

    He was the father of genetics. He is an Austrian monk who discovered the basic principles of heredity through experiments in his garden. His observation became the foundation of modern genetics and the study of heredity, and he is widely considered a pioneer in the field of genetics.

    GREGOR MENDEL

  • 2

    It is the hereditary material in humans and almost all other organisms.

    DNA OR DEOXYRIBONUCLEIC ACID

  • 3

    These are structured within cells that convert food into a form that cells can use.

    MITOCHONDRIA

  • 4

    Gene therapy is also called as?

    GENE EDITING

  • 5

    The deliberate alteration of a selected DNA sequence. It used to remove “detective” genes and replaces them with a corrected copy

    GENE THERAPY

  • 6

    An article about Gene Therapy was published in the Journal of Heredity

    1947

  • 7

    Studies on the modification and DNA transfers using virus.

    1960-1968

  • 8

    Foundational proposal and rationale for gene therapy

    1972

  • 9

    Premature and non-approved attempt at clinical Gene therapy

    1980

  • 10

    Development of adenovirus vectors

    1977-1986

  • 11

    First human gene transfer study

    1990

  • 12

    Patient dies during a trial of gene therapy

    1999

  • 13

    First regulatory approval of a gene therapy product

    2003

  • 14

    The first clinical trial utilizing electrotransfer (electroporation)

    2008

  • 15

    European Commission approves Glybera

    2012

  • 16

    Discovery and utilization of CRISPR-C

    2010-2013

  • 17

    FDA approval of Kynamro

    2013

  • 18

    First clinical trial of genome editing

    2014

  • 19

    FDA approves a first of its kind of product for the treatment of melanom

    2015

  • 20

    FDA approval of Spinraza

    2016

  • 21

    Use of “universal donor” TALEN- engineered CAR-T cells

    2017

  • 22

    FDA approval of Kymriah, Yescarta, and Luxturna

    2017

  • 23

    A genetic retina disorder that causes visual impairment beginning in infancy

    LEBER'S CONGENITAL AMAUROSIS (LCA)

  • 24

    ✓A mutation in the Dystrophin gene effects both skeletal and cardiac muscles.  ✓Most commonly inherited myopathy in childhood ✓Typically affects thighs & pelvis followed by arms ✓Trouble standing up ✓Most are unable to walk by the age of 12 ✓Gene therapy trials on mice and dogs have shown

    DUCHENNE MUSCULAR DYSTROPHY (DMD)

  • 25

    ✓ Type of cancer where the bone marrow makes too many immature lymphocytes and affects the blood chemistry ✓ FDA has approved two (2) CAR-T therapies by 2017 ✓ Patients show high remission rates after treatment

    BLOOD CANCER: ACUTE LYMPHOBLASTIC LEUKEMIA (ALL)

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    Anndrea S. Galupo · 8問 · 2年前

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    ACCOUNTING- PAS 12

    8問 • 2年前
    Anndrea S. Galupo

    FILI 101- YUNIT 2

    FILI 101- YUNIT 2

    Anndrea S. Galupo · 28問 · 2年前

    FILI 101- YUNIT 2

    FILI 101- YUNIT 2

    28問 • 2年前
    Anndrea S. Galupo

    問題一覧

  • 1

    He was the father of genetics. He is an Austrian monk who discovered the basic principles of heredity through experiments in his garden. His observation became the foundation of modern genetics and the study of heredity, and he is widely considered a pioneer in the field of genetics.

    GREGOR MENDEL

  • 2

    It is the hereditary material in humans and almost all other organisms.

    DNA OR DEOXYRIBONUCLEIC ACID

  • 3

    These are structured within cells that convert food into a form that cells can use.

    MITOCHONDRIA

  • 4

    Gene therapy is also called as?

    GENE EDITING

  • 5

    The deliberate alteration of a selected DNA sequence. It used to remove “detective” genes and replaces them with a corrected copy

    GENE THERAPY

  • 6

    An article about Gene Therapy was published in the Journal of Heredity

    1947

  • 7

    Studies on the modification and DNA transfers using virus.

    1960-1968

  • 8

    Foundational proposal and rationale for gene therapy

    1972

  • 9

    Premature and non-approved attempt at clinical Gene therapy

    1980

  • 10

    Development of adenovirus vectors

    1977-1986

  • 11

    First human gene transfer study

    1990

  • 12

    Patient dies during a trial of gene therapy

    1999

  • 13

    First regulatory approval of a gene therapy product

    2003

  • 14

    The first clinical trial utilizing electrotransfer (electroporation)

    2008

  • 15

    European Commission approves Glybera

    2012

  • 16

    Discovery and utilization of CRISPR-C

    2010-2013

  • 17

    FDA approval of Kynamro

    2013

  • 18

    First clinical trial of genome editing

    2014

  • 19

    FDA approves a first of its kind of product for the treatment of melanom

    2015

  • 20

    FDA approval of Spinraza

    2016

  • 21

    Use of “universal donor” TALEN- engineered CAR-T cells

    2017

  • 22

    FDA approval of Kymriah, Yescarta, and Luxturna

    2017

  • 23

    A genetic retina disorder that causes visual impairment beginning in infancy

    LEBER'S CONGENITAL AMAUROSIS (LCA)

  • 24

    ✓A mutation in the Dystrophin gene effects both skeletal and cardiac muscles.  ✓Most commonly inherited myopathy in childhood ✓Typically affects thighs & pelvis followed by arms ✓Trouble standing up ✓Most are unable to walk by the age of 12 ✓Gene therapy trials on mice and dogs have shown

    DUCHENNE MUSCULAR DYSTROPHY (DMD)

  • 25

    ✓ Type of cancer where the bone marrow makes too many immature lymphocytes and affects the blood chemistry ✓ FDA has approved two (2) CAR-T therapies by 2017 ✓ Patients show high remission rates after treatment

    BLOOD CANCER: ACUTE LYMPHOBLASTIC LEUKEMIA (ALL)